Table 1.
Exon Repairs in This Studya
DMD-type defect (out of frame) | exon skip target | in-frame repair edit studied | |
---|---|---|---|
Δe46–53 | exon 45 | Δe45–53 | |
exon 54 | Δe46–54 | ||
Δe47–54 | exon 46 | Δe47–55 | |
exon 55 |
Edits in this study were chosen to be alternative repairs of specific DMD-type defects.