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Description of LGMD2D cohorts at baseline
| Cohort/subject no. | Age baseline (years) | Sex | Limb infusion | Dose (vg/kg) | Baseline ambulation |
|---|---|---|---|---|---|
| 1A/E-01 | 49 | F | Single limb | 1 × 1012 right | No |
| 1B/E-02 | 9 | M | Dual limb | 1 × 1012/limb | Yes |
| 1B/E-03 | 13 | M | Dual limb | 1 × 1012/limb | Yes |
| 1B/E-04 | 8 | M | Dual limb | 1 × 1012/limb | Yes |
| 2/E-05 | 12 | M | Dual limb | 3 × 1012/limb | Yes |
| 2/E-06 | 8 | F | Dual limb | 3 × 1012/limb | Yes |
LGMD2D, limb-girdle muscular dystrophy type 2D.
