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. 2019 Oct 30;3(21):3241–3247. doi: 10.1182/bloodadvances.2019000811

Figure 1.

Figure 1.

Study design. aRecording of bleeds and FIX replacement before, and after, etranacogene dezaparvovec treatment. Assessment of bleeds and FIX replacement before screening were based on medical records. bNo e-diary recording during long-term follow-up.