Table 5.
Novel therapeutic agents that target complement activity
| Drug | Target | Mechanism | Clinical trial number |
|---|---|---|---|
| ACH-0144471 | Factor D | Prevents formation of C3 and C5 convertases | , , |
| LNP023 | Factor B | Prevents formation of C3 and C5 convertases | Not yet registered |
| APL2 | C3 | Prevents formation of C3 and C5 convertases | |
| AMY-101 | C3 | Prevents formation of C3 and C5 convertases | |
| OMS721 | MASP-2 | Blocks initiation of lectin pathway | |
| Eculizumab | C5 | Blocks progression of terminal pathway | Off-label use |
| Avacopan | C5aR1 | Blocks anaphylatoxin formation (C3a, C4a and/or C5a) |
No clinical trials of drugs that enhance complement regulation are currently ongoing in patients with C3 glomerulopathy.