AAV	Adeno-associated virus
ASO	Antisense oligonucleotide
CNS	Central nervous system
CELF1	CUGBP Elav-Like Family Member 1
CRISPR	Clustered regularly interspaced short palindromic repeat
DM	Myotonic dystrophy
DM1	Myotonic dystrophy type1
DM2	Myotonic dystrophy type 2
DMD	Duchenne muscular dystrophy
FXS	Fragile X syndrome
GalNac	N-acetyl-D-galactosamine
HD	Huntington disease
KO	Knockout
LNA	Locked nucleic acid
MBNL	Muscle blind-like proteins
miRNA	MicroRNA
2′-MOE	2′-O-methoxyethyl
mRNA	Messenger RNA
nPTB	Polypyrimidine tract-binding protein
PLGA	poly(lactide-co-glycolide)
PS	Phosphorothioate
RISC	RNA-induced silencing complex
RNAi	RNA interference
SCAs	Spinocerebellar ataxias
SCA8	Spinocerebellar ataxia type 8