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. 2020 Jan 6;2020(1):CD006282. doi: 10.1002/14651858.CD006282.pub5

Merlini 2007.

Methods Randomised, placebo‐controlled, double‐blind trial
Participants 110 participants with SMA types II or III, aged ≥ 4 years
Interventions Acetyl‐L‐carnitine 50 mg/kg/day (maximum 3 g/day) (route not mentioned) or placebo
Duration of treatment: 9 months
Follow‐up: 12 months
Outcomes Change in muscle strength arm and leg (myometry), change in functional score (time to walk 10 m and to arise from floor), change in pulmonary function (FVC), change in quality of life (Short Form‐36 Health Survey questionnaire (SF‐36) or Childhood Health Assessment Questionnaire.
Notes Study status unknown (last report on trial notified in 2007). No results available