NCT00568802.
Methods | Randomised, placebo‐controlled, double‐blind trial |
Participants | Participants with SMA types II and III, aged 1–10 years |
Interventions | Hydroxyurea (dose and route) or placebo Duration of treatment: not mentioned |
Outcomes | Motor function (Gross Motor Function Measure and timed motor tests), adverse events, pulmonary function, motor unit number estimation, SMN protein and SMN mRNA |
Notes | Study completed, not enough data or results available for analysis or inclusion (or both). Unknown date of completion, last date received 2008. |