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. 2020 Feb 7;11:51. doi: 10.1186/s13287-020-1572-7

Table 1.

Population

Number of patients
Infused patients 11
 Crigler-Najjar 6
  Type 1 5
  Type 2 1
 Urea cycle defect 5
  OTC deficiency 4
  Arginase deficiency 1
Sex
 Female 7
 Male 4
Age at infusion 0.9–16.25 year(s)
Patients per cell dosage
 12.5 × 106/kg 4
 50 × 106/kg 2
 200 × 106/kg 5
Total number of infusions 1–10
Total number of days of infusions 1–4
Completed infusion cycles 7