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. 2020 Jan 12;10(1):43. doi: 10.3390/brainsci10010043
Abnormal involuntary movements scale AIMS
Alzheimer’s disease AD
Antisense Oligonucleotide ASO
Blood-brain barrier BBB
Brain-derived neurotrophic factor BDNF
Clustered regularly interspaced short palindromic repeats-CRISPR-associated system CRISPR-Cas9
Cerebrospinal fluid CSF
Cytosine-adenine-guanine CAG
Eicosapentaenoic acid EPA
Electron transport chain ETC
Food and Drug Administration FDA
Huntington disease HD
Huntingtin gene HTT
micro RNA miRNA
Mini-mental state examination MMSE
Mutant huntingtin protein mHTT
Mammalian target of rapamycin mTOR
1-methyl-4-phenyl-1,2,3,6-tetrahydropyridine MPTP
N-methyl-D-aspartate NMDA
Parkinson’s disease PD
RNA Interference RNAi
small interfering RNA siRNA
Spinal muscular atrophy SMA
Suberoylanilide hydroxamic acid SAHA
Tauroursodeoxycholic acid TUDCA
Tetrabenazine TBZ
Total functional capacity TFC
Total motor score TMS
Unified HD rating scale UHDRS
Vesicular monoamine transporter 2 VMAT2
Zinc finger proteins ZFPs