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. 2020 Jan 31;21(3):956. doi: 10.3390/ijms21030956
α-Gal A α-galactosidase A
DGJ 1-deoxygalactonojirimycin
ERT enzyme replacement therapy
FD Fabry disease
GLP good laboratory practice
HEK human embryonic kidney cell
PBMC peripheral blood mononuclear cells