| 6MWT | six-minute walk test |
| DS | dermatan sulphate |
| ERT | enzyme replacement therapy |
| GAG | glycosaminoglycan |
| HS | heparan sulphate |
| HSCT | hematopoietic stem cell transplantation |
| IDDD | intrathecal drug delivery device |
| LSD | lysosomal storage disorder |
| MPS | mucopolysaccharidosis |
| NBS | newborn screening |
| NSC | neural stem cell |
| uGAG | urinary glycosaminoglycan |
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