AAV	Adeno-associated virus
ADL	Activity of daily living
BBB	Blood-brain barrier
BMD	Bone mineral density
BMT	Bone marrow transplantation
C6S	Chondroitin-6-sulfate
CBA	Chicken β-actin
CSF	Cerebrospinal fluid
CT	Computed tomography
D8	Aspartic acid octapeptide
DBS	Dried blood spot
DMB	Dimethylmethylene blue
ECM	Extracellular matrix
ELISA	Enzyme-linked immunosorbent assay
EMA	European Medicines Agency
ERT	Enzyme replacement therapy
FDA	Food and Drug Administration
FEV1	Forced expiratory volume in 1s
FVC	Forced vital capacity
GAG	Glycosaminoglycans
GALNS	N-acetylgalactosamine 6-sulfate sulfatase
GVHD	Graft versus host disease
HS	Heparan sulfate
HSCT	Hematopoietic stem cell transplantation
KS	Keratan sulfate
LC-MS/MS	Liquid chromatography tandem mass spectrometry
MPS	Mucopolysaccharidosis
MRI	Magnetic resonance imaging
NLC	Nanostructured lipid carriers
SDET	Substrate degradation enzyme therapy