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. 2020 Feb 14;295(13):4134–4170. doi: 10.1074/jbc.REV119.007678

Table 1.

Currently known REDs

Repeat unit Gene and position of the repeat in the gene Disease Year of discovery Highlight paper Inheritance pattern Healthy range, no. of repeats Symptomatic range, no. of repeats
ATTCT ATXN10, intron Spinocerebellar ataxia 10 (SCA10) 2000 535 Autosomal dominant 10–22 500–4500
DAB1; intron Spinocerebellar ataxia 37 (SCA37) 2017 22 Autosomal dominant <30 46–71
CAG ATXN1, coding sequence Spinocerebellar ataxia1 (SCA1) 1993 536 Autosomal dominant 6–39 41–83
ATXN2, coding sequence Spinocerebellar ataxia2 (SCA2) 1996 21, 537 Autosomal dominant <31 33–200
ATXN3, coding sequence Spinocerebellar ataxia3 (SCA3) 1994 18 Autosomal dominant <44 52–86
CACNA1A, coding sequence Spinocerebellar ataxia6 (SCA6) 1997 538 Autosomal dominant <18 20–33
TPB, coding sequence Spinocerebellar ataxia 17 (SCA17) 2001 539 Autosomal dominant 25–44 47–63
ATN1, coding sequence Dentatorubral-pallidoluysian atrophy, Naito-Oyanagi disease (DRPLA) 1994 29, 30 Autosomal dominant 6–35 49–88
HTT, coding sequence Huntington disease (HD) 1993 12 Autosomal dominant 9–29 36–121
ATXN8, coding sequence Spinocerebellar ataxia8 (SCA8) 1999 114 Autosomal dominant 15–50 71–1300
PPP2R2B, 5′ UTR Spinocerebellar ataxia 12 (SCA12) 1999 540 Autosomal dominant 7–32 51–78
ATXN7, coding sequence Spinocerebellar ataxia7 (SCA7) 1997 17 Autosomal dominant 7–17 38–130
AR, coding sequence Spinal and bulbar muscular atrophy (SBMA) 1991 10 X-linked recessive <34 >38
GLS, 5′-UTR Glutaminase deficiency (GD) 2019 470 Autosomal recessive 8–16 400–1500
CCCCGCCCCGCG CSTB, 5′-UTR Progressive myoclonus epilepsy of the Unverricht--Lundborg type (EPM1) 1997 541 Autosomal recessive 2–3 38–77
CCCTCT TAF1, intron X-linked dystonia parkinsonism (XDP) 2019 31 X-linked recessive N/A 30–60
CCTG CNBP, intron Myotonic mystrophy2 (DM2) 2001 54 Autosomal dominant <30 75–11,000
CTG DM1, 3′-UTR Myotonic mystrophy1 (DM1) 1992 11 Autosomal dominant 5–37 50–5,000
JPH3, 3′-UTR Huntington disease-like 2 2001 542 Autosomal dominant 6–28 >41
ATXN8, intron Spinocerebellar ataxia8 (SCA8) 1999 114 Autosomal dominant 15–34 90–250
TCF4, intron Fuchs endothelial corneal dystrophy 2012 543 Autosomal dominant <40 >50
GAA DMD, intron Duchenne muscular dystrophy (DMD) 2016 64 X-linked recessive 11–33 59–82
FXN, intron Friedreich ataxia 1 (FRDA) 1996 62 Autosomal recessive 5–30 >70
CGG XYLT1, 5′-UTR Baratela--Scott syndrome (BSS) 2019 544 Autosomal recessive 9–20 100–800
FMR2, 5′-UTR Mental retardation, X-linked, associated with fragile site FRAXE 1993 545 X-linked recessive 4–39 >200
DIP2B, 5′-UTR Mental retardation, associated with fragile site FRA12A 2007 546 Autosomal dominant 12–26 >150
FMR1, 5′-UTR Fragile X mental retardation syndrome 1991 59 X-linked dominant 6–52 231–2000
CBL, 5′-UTR Jacobsen syndrome 1998 547 Not inherited 11 >100
NOTCH2NLC Neuronal intranuclear inclusion disease (NIID) 2019 380 Autosomal dominant 13–30 60–959
GCN (polyAla) RUNX2, coding sequence Cleidocranial dysplasia 1997 42 Autosomal dominant 17 27
SOX3, coding sequence Mental retardation, X-linked 2002 43 X-linked recessive 11 15–26
PRDM12, coding sequence Congenital insensitivity to pain (CIP) 2015 44 Autosomal recessive 12 18–19
PABPN1, coding sequence Oculopharyngeal muscular dystrophy 1998 45 Autosomal dominant 6 7–17
HOXD13, coding sequence Synpolydactyly 1 1996 46, 47 Autosomal dominant 15 22–29
HOXA13, coding sequence Hand-foot-genital (HFG) syndrome 2000 48 Autosomal dominant 18 24–26
ARX, coding sequence Epileptic encephalopathy, early infantile, 1 2007 49, 50 X-linked recessive 10–16 17–23
PHOX2B, coding sequence Central hypoventilation syndrome, congenital 2003 51 Autosomal dominant 20 24–33
ZIC2, coding sequence Holoprosencephaly 5 2001 52 Autosomal dominant 15 25
FOXL2, coding sequence Blepharophimosis, ptosis, and epicanthus inversus syndrome 2001 53 Autosomal dominant 14 22–24
GGCCTG NOP56, intron Spinocerebellar ataxia 36 (SCA36) 2011 93 Autosomal dominant 3–14 650–2500
GGGGCC C9orf72, intron Amyotrophic lateral sclerosis and frontotemporal degeneration (ALS/FTD) 2011 37, 100 Autosomal dominant 2–19 250–1600
TGGAA BEAN1, intron Spinocerebellar ataxia 31 (SCA31) 2009 548 Autosomal dominant 26 500–760
TTTCA/TTTTA SAMD12, intron Familial adult myoclonic epilepsy1 (FAME1) 2018 67, 68 Autosomal dominant 7–20 440–3680
TNRC6A, intron Familial adult myoclonic epilepsy6 (FAME6) 2018 67, 68 Autosomal dominant 18 >22
RAPGEF2, intron Familial adult myoclonic epilepsy7 (FAME7) 2018 67, 68 Autosomal dominant 18 >22
MARCH6, intron Familial adult myoclonic epilepsy3 (FAME3) 2019 32 Autosomal dominant 9–20 791–1035
STARD7, intron Familial adult myoclonic epilepsy2 (FAME2) 2019 69 Autosomal dominant 5–35 40–1000
AAGGG RFC1, intron Cerebellar ataxia, neuropathy and vestibular areflexia syndrome 2019 291 Autosomal recessive 11 400–2000