Table 1.
Patient Characteristics
| Characteristic | Value |
|---|---|
| Age, yr | |
| Median (range) | 7.0 (.2-19.4) |
| Gender | |
| Female | 54 |
| Male | 88 |
| Underlying disease | |
| Immunedeficiency∗ | 27 |
| Leukemia/lymphoma | 60 |
| Bone marrow failure†, bone marrow disease without chemotherapy‡ | 30 |
| Inborn error of metabolism§ | 25 |
Immune deficiencies include combined immune deficiency, severe combined immune deficiency, hemophagocytic lympho histiocytosis, autoimmune lymphoproliferative syndrome, and chronic granulomatous disease. Leukemia includes acute lymphoblastic leukemia and acute myeloid leukemia.
Bone marrow failure includes Fanconi anemia, congenital agranulocytosis, and thallasemia.
Bone marrow diseases not pretreated with chemotherapy include myelodysplastic syndrome and juvenile myelomonocytotic leukemia.
Inborn errors of metabolism includes predominantly Hurler syndrome.