| AAV | adeno-associated virus |
| ASO | antisense oligonucleotide |
| CSF | cerebrospinal fluid |
| HD | Huntington’s Disease |
| HTT | Huntingtin gene |
| htt | huntingtin |
| miRNA | micro ribonucleotide acid |
| RISC | ribonucleotide acid-induced silencing |
| shRNA | Short hairpin ribonucleotide acid |
| siRNA | Small inhibitory ribonucleotide acid |
| SNP | Single nucleotide polymorphism |
| ssRNA | single-stranded ribonucleotide acid |
| UHDRS | Unified Huntington’s Disease Rating Scale |