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. 2020 Mar 20;21(6):2146. doi: 10.3390/ijms21062146
AAV adeno-associated virus
ASO antisense oligonucleotide
CSF cerebrospinal fluid
HD Huntington’s Disease
HTT Huntingtin gene
htt huntingtin
miRNA micro ribonucleotide acid
RISC ribonucleotide acid-induced silencing
shRNA Short hairpin ribonucleotide acid
siRNA Small inhibitory ribonucleotide acid
SNP Single nucleotide polymorphism
ssRNA single-stranded ribonucleotide acid
UHDRS Unified Huntington’s Disease Rating Scale