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. 2020 Apr 28;4(8):1770–1779. doi: 10.1182/bloodadvances.2020001729

Table 2.

Baseline characteristics of treatment-naïve patients treated with haplo donors

No. Age and sex Severity Clonality PNH MK Donor ABO compatibility CMV status
1 16 M SAA + 46 XY 56 M, father Matched Matched
2 25 F vSAA + 46 XX 13 F, nephew Matched Mismatched (donor +)
3 11 F vSAA 46 XX 31 M, father Minor mismatched Matched
4 4 F vSAA 46 XX 55 M, father Matched Matched
5 25 M vSAA 46 XY 54 M, father Minor mismatched Matched
6 22 F SAA + 46 XX 54 M, father Matched Matched
7 23 F SAA + 46 XX 19 M, brother Matched Matched
8 17 M* vSAA 46 XY known biallelic MPL 50 F, mother Matched Matched
9 17 M vSAA + 46 XY 48 M, father Matched Matched
10 63 F vSAA + 46 XX 34 M, son Matched Matched
11 17 M SAA + 46 XY 19 M, brother Matched Mismatched (donor +)
12 26 M vSAA + 46 XY 24 F, cousin Matched Matched
13 56 F vSAA + 46 XX 29 F, niece Matched Mismatched (donor −)
14 51 M vSAA + 46 XY 27 F, daughter Major mismatched Matched
15 20 M SAA 46 XY 41 F, mother Matched Mismatched (donor +)
16 3 F vSAA + 46 XX 40 M, father Matched Matched
17 52 M SAA + 46 XY 44 F, cousin Matched Mismatched (donor −)
*

Denotes patient with inherited SAA.