Table 2.
Baseline characteristics of treatment-naïve patients treated with haplo donors
No. | Age and sex | Severity | Clonality PNH MK | Donor | ABO compatibility | CMV status | |
---|---|---|---|---|---|---|---|
1 | 16 M | SAA | + | 46 XY | 56 M, father | Matched | Matched |
2 | 25 F | vSAA | + | 46 XX | 13 F, nephew | Matched | Mismatched (donor +) |
3 | 11 F | vSAA | − | 46 XX | 31 M, father | Minor mismatched | Matched |
4 | 4 F | vSAA | − | 46 XX | 55 M, father | Matched | Matched |
5 | 25 M | vSAA | − | 46 XY | 54 M, father | Minor mismatched | Matched |
6 | 22 F | SAA | + | 46 XX | 54 M, father | Matched | Matched |
7 | 23 F | SAA | + | 46 XX | 19 M, brother | Matched | Matched |
8 | 17 M* | vSAA | − | 46 XY known biallelic MPL | 50 F, mother | Matched | Matched |
9 | 17 M | vSAA | + | 46 XY | 48 M, father | Matched | Matched |
10 | 63 F | vSAA | + | 46 XX | 34 M, son | Matched | Matched |
11 | 17 M | SAA | + | 46 XY | 19 M, brother | Matched | Mismatched (donor +) |
12 | 26 M | vSAA | + | 46 XY | 24 F, cousin | Matched | Matched |
13 | 56 F | vSAA | + | 46 XX | 29 F, niece | Matched | Mismatched (donor −) |
14 | 51 M | vSAA | + | 46 XY | 27 F, daughter | Major mismatched | Matched |
15 | 20 M | SAA | − | 46 XY | 41 F, mother | Matched | Mismatched (donor +) |
16 | 3 F | vSAA | + | 46 XX | 40 M, father | Matched | Matched |
17 | 52 M | SAA | + | 46 XY | 44 F, cousin | Matched | Mismatched (donor −) |
Denotes patient with inherited SAA.