Table 2.
Age | Gender | DBS | LIPA variant | Genotype |
5 | Male | 1.03 | c.482del, p.Asn161Ilefs*19 | Heterozygote |
7 | Male | 0.34 | c.894G>A, p.Gln298Gln | Heterozygote |
9 | Female | 1.33 | WT | Normal |
31 | Male | 0.22 | c.894G>A, p.Gln298Gln | Heterozygote |
34 34 | Male Male | 0.37 0.51 | c.482del, p.Asn161Ilefs*19 c.482del, p.Asn161Ilefs*19 | Heterozygote Heterozygote |
DBS: Dried blood spot nmol/punch per hour; WT: Wildtype.