Table 2.
AAV copy number in tissues.
| Group assignment | AAV copy number (100vg/ng DNA) | |||
|---|---|---|---|---|
| Brain | Liver | Heart | Spleen | |
| Normal (n=4) | ND | ND | ND | ND |
| Sandhoff, untreated (n=4) | ND | ND | ND | ND |
| Sandhoff, treated (n=6) | 11.1±4.1 | 2,155±661 | 1,461±385 | ND |
ND, non-detectable.
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