Table 1.
Summary of Individual Studies Analyzed in This Manuscript
| Study | Laboratory | Study Design | Results Presented |
|---|---|---|---|
| 1 | A | weekly ASO injections, from 2/3–7 weeks of age (WT ASO-Ctrl, Mtm1−/y ASO-Ctrl, Mtm1−/y DYN101-m), 25 mg/kg | Figures 1, 2, 3, 4; Figures S1, S4, S5 |
| 2 | B | as for (1), 2nd independent cohort, 25 mg/kg | Figure 4; Figures S4 and S5 |
| 3 | A | single ASO injection at 3 weeks, analysis 1, 2, 4, 8 weeks post injection (WT ASO-Ctrl, Mtm1−/y ASO-Ctrl, Mtm1−/y DYN101-m), 25 mg/kg | Figure 2; Figures S2, S4, S5 |
| 4 | B | genetic cross cohort, analyzed at 2 weeks (WT, Mtm1−/y, Mtm1−/yDnm2+/−) | Figure 4; Figures S4 and S5 |
| 5 | A | weekly ASO injections, from 5 to 12 weeks of age (WT ASO-Ctrl, Mtm1−/y ASO-Ctrl, Mtm1−/y DYN101-m), 6.25, 12.5, and 25 mg/kg | Figure 2; Figure S3 |
| 6 | A | weekly ASO injections, from 8 to 12 weeks of age (WT ASO-Ctrl, Dnm2R465W/+ ASO-Ctrl, Dnm2R465W/+DYN101-m), 25 mg/kg | Figure S6 |