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. 2020 May 4;17:1178–1189. doi: 10.1016/j.omtm.2020.04.022

Table 1.

Summary of Individual Studies Analyzed in This Manuscript

Study Laboratory Study Design Results Presented
1 A weekly ASO injections, from 2/3–7 weeks of age (WT ASO-Ctrl, Mtm1/y ASO-Ctrl, Mtm1/y DYN101-m), 25 mg/kg Figures 1, 2, 3, 4; Figures S1, S4, S5
2 B as for (1), 2nd independent cohort, 25 mg/kg Figure 4; Figures S4 and S5
3 A single ASO injection at 3 weeks, analysis 1, 2, 4, 8 weeks post injection (WT ASO-Ctrl, Mtm1/y ASO-Ctrl, Mtm1/y DYN101-m), 25 mg/kg Figure 2; Figures S2, S4, S5
4 B genetic cross cohort, analyzed at 2 weeks (WT, Mtm1/y, Mtm1/yDnm2+/) Figure 4; Figures S4 and S5
5 A weekly ASO injections, from 5 to 12 weeks of age (WT ASO-Ctrl, Mtm1/y ASO-Ctrl, Mtm1/y DYN101-m), 6.25, 12.5, and 25 mg/kg Figure 2; Figure S3
6 A weekly ASO injections, from 8 to 12 weeks of age (WT ASO-Ctrl, Dnm2R465W/+ ASO-Ctrl, Dnm2R465W/+DYN101-m), 25 mg/kg Figure S6