| ALS | Amyotrophic lateral sclerosis |
| CSF | Cerebrospinal fluid |
| FTLD | Frontotemporal dementia |
| FUS | Fused in sarcoma |
| iPSC | human patient-derived induced pluripotent stem cell |
| MN | Motor neuron |
| NPC | Neural progenitor cells |
| PBS | Phosphate-buffered-saline |
| SOD1 | Superoxide dismutase 1 |
| TDP-43 | Transactive response DNA binding protein 43 kDA |