A1AT	Alpha 1 anti-trypsin
A1ATD	Alpha 1 anti-trypsin deficiency
AAV	Adeno-associated virus
AAVS1	Adeno-associated virus integration site 1
ABCA1	ATP-binding cassette subfamily A member 1
AdV	Adenovirus
AGT	Alanine:glyoxylate aminotransferase
AIP	Acute intermittent porphyria
ALT	Alanina aminotrasferasa
BBB	Blood brain barrier
BCNU	Bis-cloroethyl-nitrosourea
BM	Bone marrow
CAR	Coxsackie and adenovirus receptor
CAV-2	Canine adenoviral vector type 2
CF	Cystic fibrosis
CFTR	Cystic fibrosis transmembrane conductance regulator
ChAdV	Chimpanzee adenovirus
CNS	Central nervous system
CPS1D	Carbamoyl phosphate synthetase 1 deficiency
CR1	complement receptor 1
CRISPR/Cas	Clustered regularly interspaced short palindromic repeats-associated protein 9
DC	Dendritic cells
DMD	Duchenne muscular dystrophy
EBNA-1	Epstein-Barr nuclear antigen 1
EBV	Epstein-Barr virus
EF1α	Elongation factor 1 alpha
Epo	Erythropoietin
ESC	Embryonic stem cells
FGAdV	First-generation adenoviral vector
FLP	Flippase
Flt3L	FMS-like tyrosine kinase 2 ligand
FRT	Flippase recognition target
GAA	Acid alpha-glucosidase
GMP	Good manufacturing practices
HAdV	Human adenovirus
HBsAg HBV	Hepatitis B virus small surface antigen Hepatitis B virus
HC-AdV	High-Capacity adenoviral vector
HCV	Hepatitis C virus
HD-AdV	Helper-Dependent adenoviral vector
HDL	High-density lipoprotein
hmNPC	Human midbrain neuroprogenitor cells
HR	Homologous recombination
HSC	Hematopoietic stem cells
HSPG	Heparan sulphate proteoglycans
HSV	Herpes simplex virus
HV	Helper virus
HVR5	Hypervariable region V
IFN	Interferon
IgM	Immunoglobulin M
IL-6	Interleukin 6
iPSC	Induced pluripotent stem cells
ITR	Inverted terminal repeats
iu	Infection units
LDL	Low density lipoprotein
LDLR	Low density lipoprotein receptor
LRRK2	Leucine-rich repeat kinase 2
LSD MERS-CoV	Lysosomal storage disorders Middle East respiratory syndrome coronavirus
MHCI	Major histocompatibility complex class I
MOI	Multiplicity of infeciton
MPSVII	Mucopolysaccharidosis type VII
MSP-1	Merozoite surface protein 1
NAb	Neutralizing antibody
NHP	Non-human primates
OAV	Oncolytic adenovirus
PBGD	Porphobilinogen deaminase
PEI	Polyethylene glycol
PEPCK	Phosphoenolpyruvate carboxykinase
pfu	Plaque forming units
PH1	Primary hyperoxaluria type 1
PRR	Pattern recognition receptor
pTP	Pre-terminal protein
SAdV SARS-CoV-2	Simian adenovirus Severe acute respiratory syndrome coronavirus 2
SB	Sleeping beauty
TALEN	Transcription activator-like effector nucleases
TARGT	Transduced autologous restorative gene therapy
TLR	Toll-like receptor
TNFα	Tumor necrosis factor alpha
TP	Terminal protein
TRIO	Tracing the relationship of inputs and outputs
UGT1A1	Uridine diphospho-glucuronyl transferase 1A1
vg	viral genomes
VLDL	Very low density lipoprotein
vp	viral particles
ZFN	Zinc Finger Nucleases