Table 1.

Patient characteristics

SMA type	Age at treatment onset				SMN2 copy number
	< 2 y	2–5 y	6–17 y	Total	2	3	4	ND	Total
Type 1a/b	10	0	0	10	6	4	0	0	10
Type 1c	11	10	3	24	7	16	0	1	24
Type 2	9	37	43	89	5	76	3	5	89
Total	30	47	46	123	18	96	3	6	123

ND Not determined