Table 2.
Clinical characteristics in non-randomized controlled studies (non-RCT).
| China (n = 14) | Outside of China (n = 15) | p-Value | |
| Participant | 260.0 ± 775.0 | 247.9 ± 294.9 | 0.955 |
| Multicenter | 3 (21.4%) | 4 (26.7%) | 1.000 |
| Sponsor (Industry) | 2 (14.3%) | 2 (13.3%) | 1.000 |
| Single Group | 10 (71.4%) | 3 (66·7%) | 1.000 |
| Single Arm | 10 (74.4%) | 9 (60.0%) | 0.700 |
| Multicenter (n = 7) | Single Center (n = 22) | ||
| Participant | 354.3 ± 336.0 | 221.7 ± 627.0 | 0.600 |
| China | 3 (42.9%) | 11 (50.0%) | 1.000 |
| Sponsor (Industry) | 1 (14.3%) | 3 (13.6%) | 1.000 |
| Single Group | 5 (71.4%) | 15 (68.2%) | 1.000 |
| Single Arm | 5 (71.4%) | 14 (63.6%) | 1.000 |
| Sponsor (Industry) (n = 4) | Researcher (n = 25) | ||
| Participant | 299.5 ± 468.3 | 246.4 ± 590.2 | 0.866 |
| China | 2 (50.0%) | 12 (48.0%) | 1.000 |
| Multicenter | 1 (25.0%) | 6 (24.0%) | 1.000 |
| Single Group | 2 (50.0%) | 18 (72.0%) | 0.568 |
| Single Arm | 1 (25.0%) | 18 (72.0%) | 0.105 |
| Single Group (n = 20) | Parallel Group (n = 9) | ||
| Participant | 122.9 ± 170.4 | 544.6 ± 959.9 | 0.226 |
| China | 10 (50.0%) | 4 (44.4%) | 1.000 |
| Multicenter | 5 (25.0%) | 2 (22.2%) | 1.000 |
| Sponsor (Industry) | 2 (10.0%) | 2 (22.2%) | 0.568 |
| Single Arm | 18 (90.0%) | 1 (11.1%) | <0.001 |
| Single Arm (Industry) (n = 19) | Non-Randomized (n = 10) | ||
| Participant | 151.1 ± 203.5 | 448.7 ± 925.1 | 0.340 |
| China | 10 (52.6%) | 4 (40.0%) | 0.700 |
| Multicenter | 5 (26.3%) | 2 (20.0%) | 1.000 |
| Sponsor (Industry) | 1 (5.3%) | 3 (30.0%) | 0.105 |
| Single Group | 18 (94.7%) | 2 (20.0%) | <0.001 |
Data are mean ± SD or number (percentage) of patients.