Table 4.

Active clinical trials for Usher patients.

Identifier	Status	Intervention	Usher subtypes	Country
NCT02065011	NR	UshStat—lentiviral delivery of MYO7A	Usher 1B	USA, France
NCT01530659	NR	NT-501—ciliary neurotrophic factor intraocular implant	Usher types 2 and 3	USA
NCT03780257	R	QR-421a—antisense oligonucleotide to induce skipping of exon 13	Usher 2A due to mutations in exon 13	USA, Belgium, Canada, France
NCT03011541	R	Autologous bone marrow-derived stem cells	All	USA

All trials listed are for the treatment or prevention of Usher-associated retinal degeneration. R, currently recruiting; NR, not recruiting. See www.clinicaltrials.gov for further information.