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. 2019 Jul 30;55(Suppl):S5–S13. doi: 10.5045/br.2020.S002

Table 1.

Genetic prognostic markers in international prospective clinical trials of pediatric patients with acute myeloid leukemia.

Study group (protocol no.) Unfavorable prognostic markers Favorable prognostic markers
Children’s Oncology Group (AAML1831) inv(3)(q21q26.3)–MECOM-RPN1 fusion t(8;21)(q22;q22) RUNX1-RUNX1T1
t(6;9)(p23;q34.1)(DEKDEK-NUP214) inv(16)/t(16;16)(p13.1q22) CBFB-MYH11
Monosomy 7 NPM1 mutations
Monosomy 5/5q Biallelic CEBPA mutation
Monosomy 5/5q-[EGR1(5q31)deleted]
KMT2A(MLL)(11q23.3)
-t(4;11)(q21;q23)
-t(6;11)(q27;q23)
-t(10;11)(p11.2;q23)
-t(10;11)(p12;q23)
-t(11;19)(q23;p13.3)
NUP98(11p15.5)
12p: Rearrangement or loss of ETV6
t(16;21)(p11;q22)(FUS-ERG)
FLT3/ITD+with allelic ratio>0.1%
CBFA2T3-GLIS2
RAM phenotype
KAT6A (8p11.21) Fusion (10p12)(for patients who are 90 days or older)
Non-KMT2A-MLLT10 Fusions
St. Jude Children’s Hospital (AML16) DEK-NUP214 [t(6;9)] Absence of high-risk features
KAT6A-CREBBP [t(8;16)]
RUNX1-CBFA2T3 [t(16;21)]
-7, -5, 5q-, KMT2A-MLLT10 [t(6;11)]
KMT2A-MLLT4 [t(10;11)]
inv(3)(q21q26.2)
CBFA2T3-GLIS2 [inv(16)(p13.3q24.3)]
NUP98-KDM5A [t(11;12)(p15;p13)]
ETV6-HLXB [t(7;12)(q36;p13)]
NUP98-HOXA9 [t(7;11)(p15.4;p15)]
NUP98-NSD1
FLT3-ITD in combination with either NUP98-NSD1 fusion or WT1 mutation
Acute megakaryoblastic leukemia with KMT2A
rearrangements, CBFA2T3-GLIS2
[inv(16)(p13.3q24.3)], or NUP98-KDM5A
[t(11;12)(p15;p13)]
Berlin-Frankfurt-Münster Complex karyotype t(8;21)
-5 inv(16)
del(5q)-7
Abnormalities of 3q
FLT3 mutation
United Kingdom Medical Research Council (AML MRC 17) Complex karyotype t(8;21)/AML1-ETO
-5 inv(16)/t(16;16)/CBFB-MYH11
del(5q)-7
Abnormalities of 3q
FLT3 mutation