Table 2.

Overview of the outcome measures at different time points in the study

Study week	Screening	Baseline	1–11 wks	12 wks	13–23 wks	24 wks
Informed consent	●
Inclusion/exclusion criteria	●
Demographics	●
Concomitant disorders	●
Medical history	●
Medication	●
Adverse events/vital signs		●	●	●	●	●
Assessment
Blood and urine test		●				●
Height/weight		●		●		●
GMFCS		●		●		●
GMFM-88		●		●		●
K-BSID III		●		●		●
GAS		●		●		●
PedsQL		●		●		●

wks weeks, GMFCS Gross Motor Function Classification System, GMFM Gross Motor Function Measure, K-BSID III Korean Bayley Scales of Infant Development III, GAS Goal Attainment Scale, PedsQL Pediatric Quality of Life Inventory