a-d. Case-control germline rare LoF variant association analysis in pediatric MB subgroups vs pediatric controls (CEFALO) using burden tests (implemented in SKAT). P values were corrected for multiple testing using Bonferroni correction.
e-h. Case-control germline rare LoF variant association analysis in pediatric MB subgroups vs adult controls (gnomAD) using burden tests (two-sided Fisher’s Exact tests). P values were corrected for multiple testing using Bonferroni correction.
i. Case-control germline LoF burden analysis in pediatric MB vs adult controls (gnomAD).
j-l. Case-control germline LoF burden analysis in infant (j), childhood (k), and adult (1) MBSHH
vs adult controls (gnomAD).