Table 1. Transition probabilities for enzyme replacement therapy (ERT) and conventional therapy.

Pompe disease	Stages		Probabilities	Ref.
	From	To
ERT	Alive, symptomatic	Alive, symptomatic	0.33	(12)
	Alive, symptomatic	Adverse event	0.56	(29,30)
	Alive, symptomatic	Death	0.11	(12)
	Adverse event	Death	0.259	(12)
	Adverse event	Alive, symptomatic	0.741	(12)
Conventional therapy	Alive, symptomatic	Alive, symptomatic	0.08	(12)
	Alive, symptomatic	Death	0.92	(12)