Skip to main content
. 2020 Aug 10;11(8):915. doi: 10.3390/genes11080915
AAT α-1 antitrypsin
AAV adeno-associated virus
AAVR adeno-associated virus receptor
AGXT alanine-glyoxylate aminotransferase
Arg1 arginase-1
Cas CRISPR-associated gene
cccDNA covalently closed circular DNA
CRISPR clustered regularly interspaced short palindromic repeats
DNA deoxyribonucleic acid
DSB double-stranded break
HBV hepatitis B virus
HCC hepatocellular carcinoma
HCV hepatitis C virus
HDAd helper-dependent adenovirus
HIV human immunodeficiency virus
HR homologous recombination
iHLC induced hepatocyte-like cell
LTGT liver-targeted gene therapy
MLV murine leukemia virus
M-MLV Moloney murine leukemia virus
NASH non-alcoholic steatohepatitis
NHEJ nonhomologous end joining
pegRNA prime editing guide RNA
PH1 primary hyperoxaluria type 1
rAAV recombinant adeno-associated virus
rAd recombinant adenovirus
RNA ribonucleic acid
rSV40 recombinant simian virus 40
SB Sleeping Beauty
Sp Streptococcus pyogenes
St Streptococcus thermophilus
SV40 simian virus 40
TALEN transcription activator-like effector nuclease
Tag T cell antigen
TERT telomerase reverse transcriptase
UGT1A1 uridine diphosphate glucuronosyltransferase family 1 member A1
ZFN zinc-finger nuclease