Skip to main content
. Author manuscript; available in PMC: 2021 May 4.
Published in final edited form as: Adv Genet. 2020 May 4;105:293–380. doi: 10.1016/bs.adgen.2020.01.002

Table 1.

Examples of mammalian and human disease-associated misfolded proteins that have been studied in yeast.

Misfolded
protein(s)
Localization Disease Type
Huntingtin (Htt) Cytoplasmic or nuclear Huntington’s disease (HD) Heritable
α-Synuclein (αSyn) Cytoplasmic Parkinson’s disease (PD) and other synucleinopathies Mostly sporadic, sometimes heritable
Amyloid β (Aβ) Mostly extracellular Alzheimer’s disease (AD) Primarily sporadic, rarely heritable
Tau Cytoplasmic AD, frontotemporal dementia (FTD), Pick’s disease and other tauopathies Sporadic or heritable
Prion protein (PrP) Mostly extracellular Transmissible spongiform encephalopathies (TSEs) Sporadic, heritable and/or infectious
TDP-43 Cytoplasmic or nuclear Amyotrophic lateral sclerosis (ALS), FTD Sporadic or heritable
FUS Cytoplasmic or nuclear ALS Sporadic or heritable
C9orf72 Cytoplasmic ALS, FTD Heritable
Cu,Zn-superoxide dismutase (Sod1) Cytoplasmic, or mitochondrial IMSa ALS Sporadic or heritable
hnRNPA2B1, hnRNPA1 Nuclear or cytoplasmic Multisystem proteinopathy (MPS)—type of ALS Heritable
CREST Nuclear ALS Heritable
VAPB, VCP, OPTN, SETX, profilin 1 Cytoplasmic or nuclear ALS Heritable
Ataxin 2 (ATXN2) Nuclear or cytoplasmic Spinocereberral ataxia 2 (SCA), ALS, FTD Heritable
Transthyretin (TTR) Extracellular or cytoplasmic Transthyretin amyloidosis (ATTR), polyneuropathy Mostly heritable
Amylin (IAPP) Mostly extracellular Type II diabetes Sporadic

aIntramembrane space.