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. 2020 Oct 22;21(21):7819. doi: 10.3390/ijms21217819
AAV Adeno-associated virus
BMP4 Bone morphogenic protein 4
CNS Central nervous system
ER Endoplasmic reticulum
ERT Enzyme replacement therapy
FGF Fibroblast growth factor
GAG Glycosaminoglycan
GlcA Glucuronic acid
GlcNAc N-acetylglucosamine
GPC Glial restricted progenitor cell
HS Heparan sulfate
HSPG Heparan sulfate proteoglycan
IdoA Iduronic acid
iPSC Induced pluripotent stem cell
LSD Lysosomal storage disorder
MPS Mucopolysaccharidosis
NSC Neural stem cell
RNAi Ribonucleic acid interference
shRNA Short hairpin ribonucleic acid
siRNA Small interference ribonucleic acid
SRT Substrate reduction therapy