A-T |
Ataxia-Telangiectasia; |
ATM |
Ataxia-Telangiectasia mutated; |
BMT |
bone marrow transplantation; |
DSBs |
double strand breaks; |
MRN |
MRE11/RAD50/NBN; |
V(D)J |
variable (V), diversity (D) and joining (J); |
AFP |
alphafetoprotein; |
SOD |
superoxide dismutase; |
ROS |
reactive oxygen species; |
IR |
irradiation; |
IGF-1 |
insulin-like growth factor 1; |
SMRT |
small molecule read-through; |
ASO |
antisense oligonucleotides; |
CRISPR/Cas9 |
clustered regularly interspaced short palindromic repeats/CRISPR-associated protein-9; |
iPS cells |
induced pluripotent stem cells; |
HSV-1 |
Herpes simplex virus type 1 AAV: adeno-associated virus; |
HSCs |
hematopoietic stem cells; |
BMDCs |
bone marrow-derived cells; |
GFP |
green fluorescent protein; |
Allo-HSCT |
allogenic hematopoietic stem cell transplantation; |
GvHD |
graft-versus-host disease; |
EBV |
Epstein−Barr virus; |
HLA |
human leukocyte antigen; |
RIC |
reduced intensity conditioning. |