| AAV | Adeno-associated virus |
| ABC | ATP-binding cassette protein |
| AMT | Adsorptive-mediated transcytosis |
| BBB | Blood–brain barrier |
| BBBD | Blood–brain barrier disruption |
| BCRP | Breast cancer resistance protein |
| BTB | Blood–tumor barrier |
| CED | Convection-enhanced delivery |
| CNS | Central nervous system |
| CSF | Cerebrospinal fluid |
| CVO | Circumventricular organs |
| DIPG | Diffuse intrinsic pontine glioma |
| EC | Endothelial cells |
| EGFR | Epidermal growth factor receptor |
| FDA | Food and Drug Administration |
| FUS | Focused ultrasound |
| GBM | Glioblastoma miltiforme |
| GLUT1 | Glucose transporter 1 |
| HDAC | Histone deacetylase |
| IGFR | Insulin-like growth factor receptor |
| IR | Insulin receptor |
| IT | Intrathecal |
| LDLR | Low-density lipoprotein receptor |
| LRP1 | Low-density lipoprotein-related protein 1 |
| MCT1 | Monocarboxylate transporter 1 |
| MNP | Magnetic nanoparticles |
| MSC | Mesenchymal stem cells |
| MRI | Magnetic resonance imaging |
| MRP | Multidrug resistance protein |
| NSC | Neural stem cell |
| NVU | Neurovascular unit |
| NVU/BBB | Neurovascular unit/blood–brain barrier |
| PDGFR-β | Platelet-derived growth factor-β |
| P-gp | P-glycoprotein |
| PLGA | poly(lactic-co-glycolic acid) |
| RMT | Receptor-mediated transcytosis |
| TfR1 | Transferrin receptor 1 |
| TMT | Transporter-mediated transcytosis |
| VEGF | Vascular endothelial growth factor |