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. 2021 Jan 5;22(1):452. doi: 10.3390/ijms22010452
NPC Niemann–Pick disease type C
HP-β-CD 2-Hydroxypropyl-β-cyclodextrin
WT Wild type
ALT Alanine aminotransferase
AST Aspartate aminotransferase
H&E Hematoxylin & eosin
IU/L International unit per liter