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Hemophilia A Clinical Gene Therapy Trials (September 2020). Listed are the name of the gene therapy product and some of the vector details (eg, AAV vector serotype and type of vector AAV vs lentivirus), host cell type for cell-based gene therapy (eg, HSC or MSC), the phase of clinical trial development and the industry sponsor of the trial. AAV = adeno-associated viral vectors; HSC = hematopoietic stem cell; MSC = mesenchymal stem cell.
