Fig. 5.

INCEPTUS and ASPIRO—CHOP INTEND assessment scores over time. Abbreviations: CHOP INTEND = Children’s Hospital of Philadelphia Infant Test of Neuromuscular Disorders. Each symbol and dotted line represents a patient who received resamirigene bilparvovec, and the solid brown triangles with solid line represents the untreated control patient. The solid dark blue line represents the smoothed LOESS regression line fitted to the entire data for patients dosed with resamirigene bilparvovec, depicting the overall trend in the data over time for the dosed patients (20 July 2018 datacut).