| CYC | cyclophosphamide |
| CNO/CRMO | chronic recurrent multifocal osteomyelitis |
| DP | dynamic programming |
| EMA | European Medicines Agency |
| FDA | Food and Drug Administration |
| HKSJ | Hartung-Knapp-Sidik-Jonkman method |
| mKH | modified Knapp-Hartung method |
| MMF | mycophenolate Mofetil |
| NNHM | normal-normal hierarchical model |
| RAR | response adaptive randomization |