Table 1.

Patient characteristics.

	SDS (n = 99)	SDS-like (n = 11)
Age, median (range), years	10.8 (0.3–49.3)	15.6 (2.0–22.3)
Sex, n (%)
Male	61 (61.6)	10 (90.9)
Female	38 (38.4)	1 (9.1)
SDS germline mutation, n (%)
SBDS	98 (98.9)	0 (0)
DNAJC21	1 (1.0)
Myeloid neoplasm, n (%)
AML	8 (8.1)	0 (0)
MDS	7 (7.1)	0 (0)
None	84 (84.8)	11 (100)
Severe bone marrow failure, n (%)
Yes	6 (6.1)	1 (9.1)
No	93 (93.9)	10 (90.9)
Granulocyte-colony-stimulating-factor, n (%)
Yes	37 (37.4)	0 (0)
No	55 (55.6)	1 (9.1)
Not available	7 (7.1)	10 (90.9)