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. 2021 Feb 11;22(4):1815. doi: 10.3390/ijms22041815
AAV Adeno-Associated Virus
Ad Adenoviruses
ALS Amyotrophic Lateral Sclerosis
BAC Bacterial Artificial Chromosomes
BBB Blood–Brain Barrier
BDNF Brain-Derived Neurotrophic Factor
CAG Enhancer/Chicken β-Actin
CMV Cytomegalovirus
CNS Central Nervous System
CSF Cerebrospinal Fluid
DRG Dorsal Root Ganglion
EF1α Human Elongation Factor 1α
EPO Erythropoietin
FA Friedreich’s Ataxia
FDA U.S. Food and Drug Administration
FXN Frataxin
GFAP Glial Fibrillary Acidic Protein
HSV Herpes Simplex Virus
ICM Intra-Cisterna Magna
ICV Intracerebroventricular
IT Intrathecal
LCA Leber’s Congenital Amaurosis
MCK Muscle Creatine Kinase
NSE Neuron-Specific Enolase
SMA Spinal Muscular Atrophy
SYN1 Synapsin-1
YAC Yeast Artificial Chromosomes