| AAV | Adeno-Associated Virus |
| Ad | Adenoviruses |
| ALS | Amyotrophic Lateral Sclerosis |
| BAC | Bacterial Artificial Chromosomes |
| BBB | Blood–Brain Barrier |
| BDNF | Brain-Derived Neurotrophic Factor |
| CAG | Enhancer/Chicken β-Actin |
| CMV | Cytomegalovirus |
| CNS | Central Nervous System |
| CSF | Cerebrospinal Fluid |
| DRG | Dorsal Root Ganglion |
| EF1α | Human Elongation Factor 1α |
| EPO | Erythropoietin |
| FA | Friedreich’s Ataxia |
| FDA | U.S. Food and Drug Administration |
| FXN | Frataxin |
| GFAP | Glial Fibrillary Acidic Protein |
| HSV | Herpes Simplex Virus |
| ICM | Intra-Cisterna Magna |
| ICV | Intracerebroventricular |
| IT | Intrathecal |
| LCA | Leber’s Congenital Amaurosis |
| MCK | Muscle Creatine Kinase |
| NSE | Neuron-Specific Enolase |
| SMA | Spinal Muscular Atrophy |
| SYN1 | Synapsin-1 |
| YAC | Yeast Artificial Chromosomes |