| LSD | Lysosomal storage disease |
| FD | Fabry disease |
| Gb3 | Globotriaosylceramide |
| Gal A | galactosidase A |
| ERT | Enzyme replacement therapy |
| CRISPR | Clustered regularly interspaced short palindromic repeats |
| sgRNA | Single-guide RNA |
| Cas9 | CRISPR-associated protein |
| ddPCR | Droplet digital PCR |
| ESCs | Embryonic stem cells |
| iPSCs | Induced pluripotent stem cells |
| CMs | Cardiomyocytes |
| ECs | Endothelial cells |
| HUVECs | Human umbilical vein endothelial cells |
| MVEs | Multivesicular endosomes |
| AVs | Autophagic vacuoles |
| ROS | Reactive oxygen species |
| EMT | Endothelial-to-mesenchymal transition |