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. 2021 Mar 22;175(6):1–7. doi: 10.1001/jamapediatrics.2020.7140

Table 2. Budget Impact Analysis, Medicaid Perspective for US and Selected State Programs.

Estimates US Alabama Washington, DC Florida Georgia Louisiana Maryland Mississippi North Carolina South Carolina Virginia
Total No. eligible for gene therapy 5464 182 44 521 353 245 170 184 260 203 153
No. to receive therapy, year 1 383 13 3 36 25 17 12 13 18 14 11
No. treated per 100 000 members, year 1 0.52 1.41 1.18 0.96 1.36 1.11 0.90 1.99 1.02 1.37 1.04
Budget impact, year 1 (million USD), $ 707.63 23.58 5.71 67.43 45.67 31.66 22.02 23.77 33.65 26.32 19.76
Budget impact, year 1 (% total Medicaid spending) 0.12 0.42 0.20 0.29 0.41 0.29 0.19 0.45 0.25 0.42 0.21
Cost per member per month, year 1, $ 0.80 2.18 1.81 1.48 2.09 1.81 1.38 3.07 1.57 2.11 1.60
Cost per member per month, year 5, $ 0.53 1.45 1.21 0.98 1.39 1.20 0.92 2.04 1.05 1.41 1.06
Budget impact, year 5 (million USD), $ 471.25 15.70 3.80 44.91 30.42 21.09 14.67 15.83 22.41 17.53 13.16

Abbreviation: USD, US dollars.