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. 2021 Apr 1;9:657337. doi: 10.3389/fcell.2021.657337

TABLE 2.

Small molecules, inhibitor, transcription factors, and growth factors used for iPSC, ECS, and NPC differentiation and transdifferentiation.

Substance/Factor Function Differentiation step References
TGF-β RI kinase inhibitor VI
(SB-431542)
- BMP/TGF-β signaling inhibition
- Enhanced neuronal differentiation
- Induction of ventral telencephalic specification
- PSC differentiation into neuroepithelial cells
Neural induction Delli Carri et al., 2013; Nicoleau et al., 2013; Arber et al., 2015; Adil et al., 2018; Comella-Bolla et al., 2020; Grigor’eva et al., 2020; Vigont et al., 2021
Patterning Delli Carri et al., 2013
Noggin - BMP/TGF-β signaling inhibition
- PSC differentiation into neuroepithelial cells
Neural induction and patterning Delli Carri et al., 2013; Nicoleau et al., 2013; Nekrasov et al., 2016
Purmorphamine - BMP signaling inhibition
- Enhanced neuronal differentiation
Neural induction El-Akabawy et al., 2011; Adil et al., 2018
Patterning El-Akabawy et al., 2011; Nekrasov et al., 2016; Adil et al., 2018; Grigor’eva et al., 2020; Vigont et al., 2021
Maturation El-Akabawy et al., 2011
Brain-derived neurotrophic factor - Neuronal survival factor
- Increase the proportion of DARP-32-positive neurons
Patterning Zhang et al., 2010; Delli Carri et al., 2013; Lin et al., 2015; Adil et al., 2018; Grigor’eva et al., 2020
Maturation El-Akabawy et al., 2011; Delli Carri et al., 2013; Nicoleau et al., 2013; Victor et al., 2014; Arber et al., 2015; Lin et al., 2015; Nekrasov et al., 2016; Wu M. et al., 2018; Comella-Bolla et al., 2020; Grigor’eva et al., 2020; Vigont et al., 2021
Dihydrochloride (LDN-193189) - BMP/TGF-β signaling inhibition
- Induction of ventral telencephalic specification
Neural induction Arber et al., 2015; Wu M. et al., 2018; Comella-Bolla et al., 2020; Grigor’eva et al., 2020; Vigont et al., 2021
Sonic hedgehog - Induction of forebrain neurogenesis
- Promote differentiation into DARPP-32-positive neurons
Patterning Zhang et al., 2010; El-Akabawy et al., 2011; Delli Carri et al., 2013; Nicoleau et al., 2013; Lin et al., 2015
Basic fibroblast growth factor - Neuronal survival factor Neural induction Al-Gharaibeh et al., 2017
Patterning Zhang et al., 2010; Nekrasov et al., 2016; Grigor’eva et al., 2020; Vigont et al., 2021
Glial cell line-derived neurotrophic factor - Neuronal survival factor Maturation Arber et al., 2015; Lin et al., 2015; Adil et al., 2018; Wu M. et al., 2018; Vigont et al., 2021
Dorsomorphin - BMP signaling inhibition
- Enhanced neuronal differentiation
- Induction of ventral telencephalic specification
- PSC differentiation into neuroepithelial cells
Neural induction Arber et al., 2015; Nekrasov et al., 2016; Grigor’eva et al., 2020
Forskolin - cAMP pathway activator Patterning and maturation Nekrasov et al., 2016
Maturation Comella-Bolla et al., 2020; Vigont et al., 2021
Activin A - TGF-β/BMP signaling pathway activation
- Induction of forebrain neurogenesis
- Differentiation in the lateral ganglionic eminence
- Promote differentiation into DARPP-32-positive neurons
Patterning and maturation Arber et al., 2015; Grigor’eva et al., 2020
Dibutyryl-cAMP - Cell-permeable analog of cAMP
- Enhance the output of depolarized neurons
- Stimulate GABAergic MSNs neurogenesis
Maturation Zhang et al., 2010; El-Akabawy et al., 2011; Nicoleau et al., 2013; Victor et al., 2014; Lin et al., 2015; Adil et al., 2018; Grigor’eva et al., 2020
Ascorbic acid
- Formation and maintenance of the neural microenvironment
- Neuroprotective
Maturation Wu M. et al., 2018; Comella-Bolla et al., 2020; Grigor’eva et al., 2020
ROCK inhibitor
(Y-27632)
- Stem cell survival factor Neural induction Compagnucci et al., 2016; Comella-Bolla et al., 2020
Patterning Zhang et al., 2010; Delli Carri et al., 2013; Lin et al., 2015; Compagnucci et al., 2016; Grigor’eva et al., 2020
Valproic acid; Valpromide - Stimulation of GABAergic MSN neurogenesis Maturation Zhang et al., 2010; El-Akabawy et al., 2011; Nicoleau et al., 2013; Victor et al., 2014
Neurotrophin-3 - Neurotrophic factor Maturation Victor et al., 2014
Retinoid acid - Induce GABAergic differentiation Patterning and maturation El-Akabawy et al., 2011; Victor et al., 2014
WNT inhibitor dickkopf 1 - WNT signaling inhibition Patterning Zhang et al., 2010; El-Akabawy et al., 2011; Delli Carri et al., 2013; Nicoleau et al., 2013; Adil et al., 2018
Insulin - Proliferation improvement Patterning Delli Carri et al., 2013; Shahbazi et al., 2019
Maturation Delli Carri et al., 2013; Lin et al., 2015; Shahbazi et al., 2019
Insulin-like growth factor 1 - Synapse formation Maturation Lin et al., 2015; Nieto-Estévez et al., 2016; Adil et al., 2018
Tankyrase inhibitor (IWR1) - WNT signaling inhibition Neural induction and patterning Comella-Bolla et al., 2020
Tankyrase inhibitor
(XAV-939)
- WNT signaling inhibition Patterning Wu M. et al., 2018