TABLE 3.
List of companies mentioned in the text.
| Company name (Location) | Website |
|---|---|
| Abeona Therapeutics, Inc. (Dallas, TX) | https://www.abeonatherapeutics.com/ |
| Agilis Biotherapeutics Inc. (now PTC, Lynnfield, MA) | |
| Alnylam Pharmaceuticals (Cambridge, MA) | https://www.alnylam.com/ |
| Amicus Therapeutics (Cranberry, NJ) | https://www.amicusrx.com/ |
| Amsterdam Molecular Therapeutics (now uniQure, Amsterdam, Netherlands) | |
| Apic Bio Inc. (Cambridge, MA) | https://apic-bio.com/tag/gene-therapy/ |
| Aspa Therapeutics (Palo Alto, CA) | https://aspatx.com/ |
| Avexis (now Novartis Gene Therapies, Bannockburn, IL) | https://www.novartis.com/our-focus/cell-and-gene-therapy |
| AVROBIO, Inc. (Cambridge, MA) | https://www.avrobio.com/ |
| Axovant Gene Therapies Ltd. (now Sio Gene Therapies, New York, NY) | https://www.siogtx.com/?gclid=EAIaIQobChMIjtP-_-DS7QIVh4KGCh0EKQM1EAAYASAAEgJHxPD_BwE |
| Biogen (Cambridge, MA) | https://www.biogen.com/en_us/home.html |
| Brain Neurotherapy Bio, Inc. (Columbus, OH and Oakland, CA) | https://www.brainneubio.com/company |
| BridgeBio Pharma (Palo Alto, CA) | https://bridgebio.com/ |
| Ceregene (now Sangamo, San Diego, CA) | |
| CuRNA /OPKO Health (Miami, FL) | http://www.opko.com/therapeutics/opko-curna/ |
| Genzyme (now Sanofi Genzyme, Cambridge MA) | https://www.sanofigenzyme.com/ |
| Geron Corporation (Menlo Park, CA) | https://www.geron.com/ |
| Ionis Pharmaceuticals Inc. (Carlsbad, CA ) | https://www.ionispharma.com/ |
| Lysogene (France) | https://www.lysogene.com/ |
| MiNA Therapeutics Ltd. (London, UK) | https://www.minatx.com/ |
| Miragen Therapeutics Inc. (Boulder, CO) | https://www.miragen.com/ |
| Neurocrine Biosciences (San Diego, CA) | https://www.neurocrine.com/ |
| nLife Therapeutics, S.L. (Granada, Spain) | https://www.n-life.es/ |
| Noxxon Pharma (Germany) | https://www.noxxon.com/ |
| Ovid Therapeutics (New York, NY and Cambridge, MA) | https://www.ovidrx.com/science/approach/ |
| ProQR Therapeutics NV (Leiden, Netherlands) | https://www.proqr.com/ |
| PTC (South Plainfield, NJ) | https://www.ptcbio.com/ |
| REGENXBIO (Rockville, MD) | https://www.regenxbio.com/ |
| Regulus Therapeutics Inc. (Carlsbad, CA) | http://www.regulusrx.com/ |
| Roche (Basel, Switzerland) | https://www.roche.com/ |
| Sangamo Therapeutics, Inc. (Richmond, CA) | https://www.sangamo.com/genomic-medicines |
| Sarepta Therapeutics (Cambridge, MA) | https://www.sarepta.com/ |
| Stoke Therapeutics (Bedford, MA) | https://www.stoketherapeutics.com/ |
| Stride Bio Inc. (Durham, NC) | https://www.stridebio.com/ |
| Taysha Gene Therapies (Dallas, TX) | https://www.tayshagtx.com/ |
| TriLink Biotechnologies Inc. (San Diego, CA) | https://www.trilinkbiotech.com/ |
| UniQure Biopharma (Lexington, MA) | http://www.uniqure.com/ |
| Voyager Therapeutics (Cambridge, MA) | https://www.voyagertherapeutics.com/ |
| Wave Life Sciences USA, Inc. (Cambridge, MA) | https://www.wavelifesciences.com/ |