TABLE 1.

Clinical and demographic characteristics of the study cohort ^a

Age at onset (years)	7.50 ± 6.02; 6.5 (1.00‐16)
Sex (M/F)	5/3
Age at treatment (years)	43.13 ± 15.25; 42 (18‐72)
Disease duration (years)	35.88 ± 15.88; 36 (4‐62)
Ambulators (yes/no)	2/6
Revised upper limb module at baseline	17.9 ± 14.8; 16 (0‐37)
Hammersmith Functional Motor Scale―Expanded	15.63 ± 22.15; 4 (0‐61)

^aData expressed as mean ± standard deviation; median (range).