Table 2.
Base case Q-TWiST analysis for patients receiving CPX-351 or 7 + 3
| Mean (SD) duration of health state, days | Means difference (95% CI), days | ||
|---|---|---|---|
| CPX-351 (n = 153) | 7 + 3 (n = 156) | ||
| Health state | |||
| TOX | 192 (356) | 185 (273) | 7 (− 63, 78) |
| TWiST | 356 (635) | 174 (451) | 183 (60, 306) |
| REL | 31 (96) | 9 (34.5) | 22 (5, 38) |
| Q-TWiST | 468 (623) | 271 (449) | 197 (76, 319) |
| Relative Q-TWiST gain | 53.6% | ||
Q-TWiST, Quality-adjusted Time Without Symptoms of disease or Toxicity; SD, standard deviation; CI, confidence interval; TOX, time with any grade 3 or 4 adverse events or before relapse; TWiST, time in remission without relapse or grade 3 or 4 adverse events; REL, time after relapse