Table 2.
Number of diseases and medicinal products per category
| Number | |
|---|---|
| Diseases | |
| Total | 134 |
| Metabolic/inborn errors | 40 |
| Neurologic | 20 |
| Hematologic | 24 |
| Inflammatory | 23 |
| Endocrine | 11 |
| Pulmonary | 5 |
| Immunologic | 2 |
| Miscellaneous | 9 |
| Medicinal products | |
| Total medicinal products (MP) | 204 |
| Drugs | 125 |
| Biologics | 79 |
| MP for metobolic diseases | 51 |
| MP for neurologic diseases | 34 |
| MP for hematologic diseases | 43 |
| MP for inflammatory diseases | 28 |
| MP for endocrine diseases | 15 |
| MP for pulmonary diseases | 22 |
| MP for immunologic diseases | 3 |
| MP for miscellaneous | 9 |
| MP used to treat multiple diseases | 6 |
| MP approved by the FDA | 139 |
| MP approved by the EMA | 160 |
| MP approved by the NMPA | 51 |
| MP on the WHO list of essential medicines (2019) | 25 |
Summary of the total number of listed diseases, the number of diseases per category, the number of total medicinal products, the number of drugs and biologics, the number of medicinal products per disease category, the number of medicinal products treating multiple diseases, and the number of medicinal products approved in each jurisdiction