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Skipping of Normal Out-of-frame Exons.
| Disease | Gene | Exon | Phase | Author, Year |
|---|---|---|---|---|
| DMD | DMD | 51, 53, 45 | A, W, I/II | Schneider et al. 2021 (25) |
| Dysferlinopathy | DYSF | 51 | P | Verwey et al. 2020 (23) |
| Parkinson’s disease | PRKN | 4 | P | Li et al. 2020 (24) |
DMD: Duchenne muscular dystrophy; A: approved; W: wait for approval; P: preclinical study
