Table 1:
Compassionate Programs and Other Treatment Support Options
| Treatment (Trade name/Manufacturer) | Type* | Company/Organization | Link |
|---|---|---|---|
| Imiglucerase (Cerezyme) | Compassionate Use/Copay assistance | Sanofi-Genzyme) | https://www.cerezyme.com/access-copay-assistance |
| Velaglucerase alfa (VPRIV) | Compassionate Use/Copay assistance | Takeda | https://www.vpriv.com/patient-support/onepath-product-support |
| Taliglucerase alfa (Elelyso) | Compassionate Use/Copay assistance | Pfizer | https://www.elelyso.com/personal-support |
| Eliglustat (Cerdelga) | Compassionate Use/Copay assistance | Sanofi-Genzyme | https://www.cerdelga.com/patient-support-and-resources |
| Miglustat (Zavesca) | Compassionate Use/Copay assistance | Actelion | https://zavesca.com/patient-patient-support.html |
| Non-specific | Copay assistance | National Gaucher Foundation (NGF) | https://www.gaucherdisease.org/financial-support/care-program/ |
| Non-specific | Copay assistance | National Organization of Rare Diseases (NORD) | https://rarediseases.org/wp-content/uploads/2020/11/Gaucher-PAP-FAQ-10-2020.pdf |
| Non-specific | Copay assistance/Expanded access | International Gaucher Alliance (IGA) | https://gaucheralliance.org/gb/about_iga/humanitarian_aid |