Table 1.

Patient characteristics (N = 30) and number of samples of DBS

Characteristic			Value
Male sex				21 (70%)
Age at pre-HCT collection, median (range), y				1.1 (0.1-4.7)
Age at transplantation, median (range), y				1.3 (0.2-4.8)
Enzyme activity level post-HCT in normal range				28 (93%)
MPS type	DBS (n)
	Pre	1-year FU	3-year FU	10-year FU
MPS	22	14	15	10
MPS 1	16	14	15	10
MPS 2	2
MPS type 3	2
MPS 6	2

FU, follow-up.