Table 1.

Patient and transplant characteristics

Number of patients	41
Median age (years)	2.3 (0.3–19.8)
Male	37
Female	4
Diagnosis
Wiskott-Aldrich syndrome	12
HLH/XLP	10
CD40 ligand deficiency	7
IPEX	2
Combined immune deficiency	2
IL-10Rb deficiency	1
Early-onset IBD	1
Lnterferon-γ receptor type 1 deficiency	1
Severe congenital neutropenia	1
X-linked SCID	1
Leukocyte adhesion deficiency type 3	1
X-linked moesin-associated immunodeficiency	1
CTLA-4 haploinsufficiency	1
Serotherapy
Alemtuzumab	32
Anti-thymocyte globulin	7
None	2
Patient/donor HLA match and relation
Matched related donor	11
Matched unrelated donor	23
1–2 allele mismatched unrelated donor	5
2–5 allele mismatched related donor	2
Graft source
Bone marrow	36
Peripheral blood stem cells	4
Cord blood	1
Graft cell dose
Total nucleated cells/kg × 108 (range)	7.7 (0.8–20.0)
CD34+ stem cells/kg × 106 (range)	9.6 (1.6–100.4)

IBD, inflammatory bowel disease; IPEX, immune dysregulation, polyendocrinopathy, enteropathy, X-linked; SCID, severe combined immune deficiency; primary HLH, hemophagocytic lymphohistiocytosis; XLP, X-linked lymphoproliferative disorder